A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
PHASE3
The primary objective of this study is to compare the effect of mitapivat v...
Status
Recruiting
Location
Weill Cornell Medical College/ New York Presbyterian
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia
PHASE3
The primary objective of this study is to compare the effect of mitapivat v...
A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Regularly Transfused, Followed by a 5-Year Extension Period
PHASE3
ACTIVATE-KidsT (AG348-C-022) is a multicenter study designed to evaluate th...
A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Not Regularly Transfused, Followed by a 5-Year Extension Period
PHASE3
Study ACTIVATE-Kids (AG348-C-023) will evaluate the efficacy and safety of ...